利用CRISPR基因编辑技术纠正Duchenne型肌营养不良症

利用CRISPR基因编辑技术，科学家在美国和德国一直在努力建立Duchenne型肌营养不良症（Duchenne muscular dystrophy，DMD）基因突变的纠正技术。科学家们说，他们用CRISPR方法比目前的方法在纠正这种疾病的遗传基础方面更简单也更有效。

"The large size and complicated structure of the DMD gene contribute to its high rate of spontaneous mutation," the scientists write in their paper, which was published in Science Advances yesterday.

见：

CRISPR Offers New Attack on Muscular Dystrophy

CRISPR Offers New Line of Attack on Muscular Dystrophy